
Clinical Outcomes Among Patients With Sickle Cell Disease and Transfusion-Dependent Beta-Thalassemia Treated With ...
Background Sickle cell disease (SCD) and beta-thalassemia are among the most common inherited monogenic disorders globally.1 It is estimated that 5.0%–7.0% of the world’s population is a carrier of a significant hemoglobin variant.2 Despite great progress …